The World Orphan Drug Congress USA is a premier event focusing on rare diseases and orphan drugs, gathering top industry leaders, healthcare professionals, and patient advocacy groups. It serves as a vital platform to discuss advancements in drug development, regulatory insights, and market access strategies, aiming to enhance treatment options and accessibility for rare disease patients. This conference provides opportunities for networking, learning, and collaboration among stakeholders, promoting innovation and improvements in healthcare outcomes for those affected by rare diseases.